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Unlocking Tomorrows Together

BioMarin continues its more than 25-year history of working towards developing first- or best-in-class therapies for people with rare genetic diseases. Our first approved therapy was inspired by a father who refused to accept that his son’s rare diagnosis lacked a viable therapy. That relentless pursuit to change the course of his son’s future through the power of treatment is still at the core of who we are today.

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Diseases & Conditions

We focus on rare conditions where we believe we can make a meaningful impact.

Learn More about the diseases and conditions we treat
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About Us

Patients are our purpose. Science is our passion.


Learn More about us