Unlocking Tomorrows Together
BioMarin continues its more than 25-year history of working towards developing first- or best-in-class therapies for people with rare genetic diseases. Our first approved therapy was inspired by a father who refused to accept that his son’s rare diagnosis lacked a viable therapy. That relentless pursuit to change the course of his son’s future through the power of treatment is still at the core of who we are today.
Diseases & Conditions
We focus on rare conditions where we believe we can make a meaningful impact.
Learn More about the diseases and conditions we treat ⌃
Our Pipeline
Each drug candidate we pursue is guided by a fundamental understanding of the genetics and underlying biology of the condition we hope to address.
Learn More about our pipline ⌃Manufacturing Excellence
We take pride in manufacturing complex therapies for the patients who need them most.
Learn More Manufacturing Excellence ⌃